Submitted by 29PiecesOfSilver t3_yqxoei in science
[deleted] t1_ivubudo wrote
Reply to comment by bigglyboblee in In a first, doctors treat fatal genetic disease before birth by 29PiecesOfSilver
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bigglyboblee t1_ivv2xio wrote
You can read the paper if you’re interested, from my skim she has to receive injections every couple weeks for the rest of her life.
I don’t see how a single dose would work for enzyme replacement therapy, but I am not an expert in this topic.
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